Rhythm Pharmaceuticals Releases Preliminary Data on Prader-Willi Syndrome Trial
Rhythm Pharmaceuticals announced preliminary data from a Phase 2 trial evaluating setmelanotide in patients with Prader-Willi syndrome delivered during the Endocrine Society's Annual Meeting in Chicago. Key highlights include: Patients with PWS treated with setmelanotide therapy achieved clinically meaningful BMI or BMI z-score reductions, reductions in fat mass with preservation of lean mass, and improvements in hyperphagia and anxiety measures; Positive results reinforce rationale for Phase 3 development of MC4R agonism in PWS
